CABL001X2101 = A Phase I, Multicenter, Open-label Study of Oral ABL001 in Patients With CML or Ph+ ALL [Asia, Australia, Europe]

Study title

CABL001X2101 = A Phase I, Multicenter, Open-label Study of Oral ABL001 in Patients With CML or Ph+ ALL [Asia, Australia, Europe]

Scientific title

A Phase I, Multicenter, Open-label Study of Oral ABL001 in Patients With Chronic Myelogenous Leukemia (CML) or Philadelphia Chromosome-positive Acute Lymphoblastic Leukemia (Ph+ ALL) (EudraCT 2013-004491-36, ClinicalTrials.gov NCT02081378)

Type of study

Trial after therapy failure or intolerance

Current status

No longer recruiting

What is the purpose of the study

This first-in-human, open label, dose finding study is conducted to establish a safe and tolerated dose of ABL001 in CML and Ph+ ALL patients who are relapsed or resistant to or are intolerant of TKIs. In these patients, ABL001 may provide a novel therapeutic option.
ABL001 capsules will be administered orally in a dose escalation schedule.

Key inclusion criteria

Patients 18 years and older with Philadelphia chromosome-positive CML in chronic or accelerated phase who were previously treated with two different tyrosine kinase inhibitors (TKIs) and are relapsed, resistant to or intolerant of TKIs.
Adult patients with cytopathologically confirmed Ph+ ALL who are relapsed or resistant to one prior TKI or intolerant of TKIs.
TKI failure for Ph+ ALL patients is defined as at least the loss of Molecular Response (MR) 4.5 (BCR-ABL ≤ 0.0032%).

Key exclusion criteria

Where can I find additional information

Study description in the US register ClinicalTrials.gov, a service of the U. S. National Institutes of Health

Study sponsor

Novartis Pharmaceuticals

Scientific lead / contact

Novartis Pharmaceuticals

Principal investigator

For Germany:
Prof. Dr. Oliver Ottmann
Universitätsklinikum Frankfurt

Study centers / principal investigators

Australia, South Australia
Adelaide, 5000
Novartis Investigative Site

France
Bordeaux, 33076
Novartis Investigative Site

Paris, Cedex 10, 75475
Novartis Investigative Site

Germany
Charité
13353 Berlin

Universitätsklinikum Frankfurt
60590 Frankfurt

Universitätsklinikum Jena
Klinik für Innere Medizin II. Abteilung Hämatologie und Internistische Onkologie
07743 Jena

Italy
Roma, 00161
Novartis Investigative Site

Japan
Kobe-city, Hyogo, 650-0017
Novartis Investigative Site

Korea, Republic of
Seoul, 137-701
Novartis Investigative Site

Netherlands
Amsterdam, 1081 HV
Novartis Investigative Site

Singapore
Singapore, 28006
Novartis Investigative Site

Spain
Madrid, 28006
Novartis Investigative Site

USA
Massachusetts
Dana Farber Cancer Institute
Hematology / Oncology
Boston, 02215

Michigan
University of Michigan Comprehensive Cancer Center SC
Ann Arbor, 48109-0944

New York
Memorial Sloan Kettering Cancer Center
New York, 10065

Oregon
Oregon Health & Science University SC-6
Portland, 97239

Texas
University of Texas
MD Anderson Cancer Center
Houston, 77030-4009

Utah
University of Utah
Huntsman Cancer Institute
Salt Lake City, 84112